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Agios reports results from late-stage study of its thalassemia treatment (NASDAQ:AGIO)

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- Agios Pharmaceuticals (NASDAQ:AGIO) presented positive results from late-stage study investigating mitapivat, an oral, small molecule PK activator, in adults with transfusion-dependent alpha- or beta-thalassemia.
- Stock is down 7% premarket.
- Mitapivat demonstrated a statistically significant reduction in transfusion burden vs placebo
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